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Late Breaking News
15 September 2022
PLENARY
•
15-PM-PLENARY-1
•
14:00
>
15:00
•
Late Breaking News
•
Apollon Auditorium
14:00
•
S18L1
•
Update on the development of Givinostat in DMD
>
P.
Paolo Umberto
BETTICA
(Cinisello Balsamo, Italy)
14:15
•
S18L2
•
An AAV-ShRNA DUX4-based therapy to treat FacioScapuloHumeral muscular Dystrophy (FSHD)
>
J.
Julie
DUMONCEAUX
(London, Uk)
14:30
•
S18L3
•
CD38-NADase is a major contributor to DMD phenotype
>
S.
Sabine
DE LA PORTE
(Montigny-Le-Bretonneux, France)
14:45
•
S18L4
•
Severe mitochondrial dysfunctions caused by a heterozygous DES mutation in iPSC-derived cardiomyocytes
>
Y.
Yeranuhi
HOVHANNISYAN
(Angers, France)
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